Velaglucerase alfa:
Gaucher disease, caused by deficiency of the enzyme glucocerebrosidase, results in accumulation of a toxic glycolipid substrate, called glucocerebroside. Velaglucerase alfa supplements or replaces beta-glucocerebrosidase, the enzyme that catalyzes the hydrolysis of glucocerebroside, reducing the amount of accumulated glucocerebroside and correcting the pathophysiology of Gaucher disease.
source:centerwatch.com
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